Details of the Drug

General Information of Drug (ID: DMR09IH)

Drug Name

SRP-9001

Indication

Disease Entry	ICD 11	Status	REF
Duchenne dystrophy	8C70	Phase 2	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

Molecular Interaction Atlas (MIA)

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Molecular Expression Atlas of This Drug

The Studied Disease

Duchenne dystrophy

ICD Disease Classification

8C70

Molecule Name	Molecule Type	Gene Name	p-value	Fold-Change	Z-score
Dystrophin (DMD)	DTT	DMD	1.15E-07	-1.07	-2.94

Molecular Expression Atlas (MEA)

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References

1	ClinicalTrials.gov (NCT03769116) A Randomized, Double-blind, Placebo-controlled Study of SRP-9001 for Duchenne Muscular Dystrophy (DMD). U.S. National Institutes of Health.
2	Clinical pipeline report, company report or official report of Sarepta Therapeutics.