General Information of Drug (ID: DMR09IH)

Drug Name
SRP-9001 Drug Info
Indication
Disease Entry ICD 11 Status REF
Duchenne dystrophy 8C70 Phase 2 [1]
Cross-matching ID
TTD Drug ID
DMR09IH

Molecule-Related Drug Atlas

Molecule-Related Drug Atlas
Molecule Type:
DTT
Drug Status:
Clinical Trial Drug(s)
Drug(s) Targeting Dystrophin (DMD)
Drug Name Drug ID Indication ICD 11 Highest Status REF
Fordadistrogene movaparvovec DMZ3X7F Duchenne muscular dystrophy 8C70.1 Phase 3 [3]
WVE-210201 DMHXJ68 Duchenne dystrophy 8C70 Phase 2/3 [4]
MyoDys DMHO6XP Duchenne dystrophy 8C70 Phase 1 [5]
Biostrophin DMS4P6K Duchenne dystrophy 8C70 Phase 1 [6]

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas

Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Dystrophin (DMD) TT48MP6 DMD_HUMAN Replacement [2]

References

1 ClinicalTrials.gov (NCT03769116) A Randomized, Double-blind, Placebo-controlled Study of SRP-9001 for Duchenne Muscular Dystrophy (DMD). U.S. National Institutes of Health.
2 Clinical pipeline report, company report or official report of Sarepta Therapeutics.
3 ClinicalTrials.gov (NCT05689164) Long-term Follow-up Safety and Efficacy Study in Participants With Duchenne Muscular Dystrophy Who Have Received Fordadistrogene Movaparvovec in a Preceding Clinical Study. U.S.National Institutes of Health.
4 Clinical pipeline report, company report or official report of the Pharmaceutical Research and Manufacturers of America (PhRMA)
5 Trusted, scientifically sound profiles of drug programs, clinical trials, safety reports, and company deals, written by scientists. Springer. 2015. Adis Insight (drug id 800009280)
6 Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches. Nat Rev Genet. 2013 Jun;14(6):373-8.