Details of Disease | DrugMAP

General Information of Disease (ID: DISVF7U7)

Disease Name	Sanfilippo syndrome
Disease Class	5C56: Lysosomal disease
Disease Hierarchy	DIS01GPL: Grass pollen hypersensitivity DISVF7U7: Sanfilippo syndrome
ICD Code	ICD-11 ICD-11: 5C56.3Y Expand ICD-11 '5C56.3Y
Disease Identifiers	MESH ID D009084 MedGen ID 6452 Orphanet ID 581 SNOMED CT ID 88393000

Drug-Interaction Atlas (DIA) of This Disease

Drug-Interaction Atlas (DIA)

This Disease is Treated as An Indication in 3 Clinical Trial Drug(s)

Drug Name	Drug ID	Highest Status	Drug Type	REF
HGT-1410	DMHZ4JI	Phase 2	NA	[1]
SHP610	DMAJZEF	Phase 2	NA	[2]
SOBI003	DMXNTR7	Phase 1/2	Recombinant protein	[3]
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Molecular Interaction Atlas (MIA) of This Disease

Molecular Interaction Atlas (MIA)

References

1	ClinicalTrials.gov (NCT02350816) Safety and Efficacy Study for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. U.S. National Institutes of Health.
2	Clinical pipeline report, company report or official report of the Pharmaceutical Research and Manufacturers of America (PhRMA)
3	ClinicalTrials.gov (NCT03811028) A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients. U.S. National Institutes of Health.