Details of the Drug-Related molecule(s) Interaction Atlas

General Information of Drug (ID: DMGKYAE)

Drug Name
AT-GTX-501 Drug Info
Indication
Disease Entry ICD 11 Status REF
CLN6 disease 5C56.1 Phase 1/2 [1]
Cross-matching ID
TTD Drug ID
DMGKYAE

Molecular Interaction Atlas of This Drug

Molecular Interaction Atlas
Download the Complete Interaction Atlas for Visualization in Cytoscape

Drug Therapeutic Target (DTT)
DTT Name DTT ID UniProt ID MOA REF
Ceroid-lipofuscinosis neuronal protein 6 (CLN6) TTJCOQ7 CLN6_HUMAN Not Available [1]

References

1 ClinicalTrials.gov (NCT02725580) Phase I/IIa Gene Transfer Clinical Trial for Variant Late Infantile Neuronal Ceroid Lipofuscinosis, Delivering the CLN6 Gene by Self-Complementary AAV9. U.S.National Institutes of Health.