Details of the Drug

General Information of Drug (ID: DMGKYAE)

Drug Name

AT-GTX-501

Indication

Disease Entry	ICD 11	Status	REF
CLN6 disease	5C56.1	Phase 1/2	[1]
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Drug Type

Gene therapy

Cross-matching ID

Molecular Interaction Atlas of This Drug

Drug Therapeutic Target (DTT)

DTT Name	DTT ID	UniProt ID	MOA	REF
Ceroid-lipofuscinosis neuronal protein 6 (CLN6)	TTJCOQ7	CLN6_HUMAN	Not Available	[1]

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Molecular Interaction Atlas (MIA)

Jump to Detail Molecular Interaction Atlas of This Drug

References

1	ClinicalTrials.gov (NCT02725580) Phase I/IIa Gene Transfer Clinical Trial for Variant Late Infantile Neuronal Ceroid Lipofuscinosis, Delivering the CLN6 Gene by Self-Complementary AAV9. U.S.National Institutes of Health.